About Rarebase

Rarebase is a public benefit precision medicine company that leverages cutting-edge technology and biology to discover and develop treatments for the millions of people worldwide living with a rare disease.

The Function platform discovers drugs that address underlying disease biology, at scale.

1. PREDICTION

We match genetic disorders with thousands of therapeutic candidates using our functional genomics screening platform.

2. DISEASE MODELS

We create cell-based disease models directly from patients’ samples.

3. VALIDATION

We test therapeutic candidates in patient cell models for therapeutic effects, such as making a functional gene copy compensate for a dysfunctional one.

4. LEARNING

We use validation data from the disease models to improve the Function platform’s predictions.